1 completed, 1 recruiting. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Recruiting 1 |
| Phase 2 | 1 | Recruiting 1 |
Follow Porphyria, Erythropoietic: new trials by email Literature Review of Porphyria, Erythropoietic trials Research Report on Porphyria, Erythropoietic
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study to Investigate the Improvement of Photosensitivity in Terms of Skin Lesions Associated With CEP Following Administration of Oral ATL-001 (Ciclopirox Oral Solution) in Participants Aged >18 Years of Age With CEP ATL-001 (Ciclopirox oral solution) - Congenital Erythropoietic Porphyria (CEP) | Phase 1 / Phase 2 | Recruiting | Atlas Molecular Pharma | 6 | 2026-01-29 | 2026-03-24 |
| Diagnostic and Screening Study of Genetic Disorders Tay-Sachs Disease, Porphyria, Erythropoietic | Completed | National Center for Research Resources (NCRR) | 50 | 1999-12-01 | 2005-06-24 |
Leukodystrophy, Globoid Cell (1) · Metabolism, Inborn Errors (1) · Tay-Sachs Disease (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Metabolic Diseases (2) · Nutritional and Metabolic Diseases (2) · Porphyrias (2) · Skin Diseases (2) · Skin Diseases, Genetic (2) · Skin and Connective Tissue Diseases (2) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Central Nervous System Diseases (1) · Demyelinating Diseases (1) · Gangliosidoses (1) · Gangliosidoses, GM2 (1)
Ciclopirox (1)
Atlas Molecular Pharma (1) · National Center for Research Resources (NCRR) (1)
United States (2)