1 terminated. 1 Phase 2, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 1 | Terminated 1 |
| Phase 3 | 1 | Terminated 1 |
Follow Pmm2-CDG: new trials by email Literature Review of Pmm2-CDG trials Research Report on Pmm2-CDG
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Acetazolamide Efficacy in Ataxia in PMM2-CDG Placebo, Acetazolamide - Pmm2-CDG, CDG1A | Phase 2 / Phase 3 | Terminated | Mayo Clinic | 25 | 2021-03-17 | 2025-03-20 |
Congenital disorder of glycosylation type 1A (1)
Acetazolamide (1) · Gelatin (1) · Lactose (1)
Mayo Clinic (1)
United States (1)