Molybdenum cofactor deficiency: Clinical Trials

1 trial for Molybdenum cofactor deficiency, newest first

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1 completed. 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1

Follow Molybdenum cofactor deficiency: new trials by email Literature Review of Molybdenum cofactor deficiency trials Research Report on Molybdenum cofactor deficiency

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Phase 1 Single Dose Study of ALXN1101 in Healthy Volunteers
ALXN1101, Placebo - Molybdenum Cofactor Deficiency (MoCD), Rare Autosomal Recessive Disorder
Phase 1CompletedOrigin Biosciences242013-06-012019-03-19

Interventions

nulibry (1)

Sponsors

Origin Biosciences (1)

Countries

United States (1)

Top investigators

Ronald Goldwater, MD (1)