nulibry: Clinical Trials

2 trials of nulibry, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 completed, 1 withdrawn. 2 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 12Completed 1, Withdrawn 1
Phase 21Withdrawn 1

Follow nulibry: new trials by email Literature Review of nulibry trials Research Report on nulibry

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Phase 1 Single Dose Study of ALXN1101 in Healthy Volunteers
ALXN1101, Placebo - Molybdenum Cofactor Deficiency (MoCD), Rare Autosomal Recessive Disorder
Phase 1CompletedOrigin Biosciences242013-06-012019-03-19
Study of cPMP (Precusor Z) to Treat Molybdenum Cofactor Deficiency (MoCD) Type A
cPMP - Molybdenum Cofactor Deficiency Type A
Phase 1 / Phase 2WithdrawnOrphatech Pharmaceuticals, GmbH102009-08-012011-02-01

Conditions studied

Molybdenum Cofactor Deficiency, Complementation Group A (1)  ·  Molybdenum cofactor deficiency (1)

Sponsors

Origin Biosciences (1)  ·  Orphatech Pharmaceuticals, GmbH (1)

Countries

Australia (1)  ·  United States (1)

Top investigators

Alex Veldman, MD (1)  ·  Ronald Goldwater, MD (1)