3 completed. 3 Phase 1, 2 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 3 | Completed 3 |
| Phase 2 | 2 | Completed 2 |
Follow Metachromatic Leukodystrophy (MLD): new trials by email Literature Review of Metachromatic Leukodystrophy (MLD) trials Research Report on Metachromatic Leukodystrophy (MLD)
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| An Efficacy and Safety Study of HGT-1110 in Participants With Metachromatic Leukodystrophy HGT-1110 - Metachromatic Leukodystrophy (MLD) | Phase 1 / Phase 2 | Completed | Shire | 24 | 2013-05-23 | 2026-04-21 |
| Multicenter Study of HGT-1110 Administered Intrathecally in Children With Metachromatic Leukodystrophy (MLD) Recombinant human arylsulfatase A - Metachromatic Leukodystrophy (MLD) | Phase 1 / Phase 2 | Completed | Shire | 24 | 2012-02-02 | 2021-06-14 |
| Metazym for the Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD) rhASA - Dose Level 1, rhASA - Dose Level 2, rhASA - Dose Level 3 - Metachromatic Leukodystrophy (MLD) | Phase 1 | Completed | Shire | 13 | 2007-01-22 | 2021-06-25 |
Leukodystrophy, Metachromatic (3)
Brain Diseases (3) · Brain Diseases, Metabolic (3) · Brain Diseases, Metabolic, Inborn (3) · Central Nervous System Diseases (3) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Demyelinating Diseases (3) · Genetic Diseases, Inborn (3) · Hereditary Central Nervous System Demyelinating Diseases (3) · Leukoencephalopathies (3) · Lipid Metabolism Disorders (3) · Lipid Metabolism, Inborn Errors (3) · Lipidoses (3) · Lysosomal Storage Diseases (3) · Lysosomal Storage Diseases, Nervous System (3) · Metabolic Diseases (3)
Shire (3)
Denmark (3) · Australia (2) · France (2) · Germany (2) · Japan (2) · Brazil (1) · Czechia (1)