Lipoprotein Lipase Deficiency: Clinical Trials

1 trial for Lipoprotein Lipase Deficiency, newest first

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1 completed. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Completed 1

Follow Lipoprotein Lipase Deficiency: new trials by email Literature Review of Lipoprotein Lipase Deficiency trials Research Report on Lipoprotein Lipase Deficiency

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
The Approach Open Label Study: A Study of Volanesorsen (Formerly IONIS-APOCIIIRx) in Participants With Familial Chylomicronemia Syndrome
Volanesorsen - Familial Chylomicronemia Syndrome, Lipoprotein Lipase Deficiency
Phase 3CompletedAkcea Therapeutics682015-12-232021-08-26

Narrower conditions

Familial hyperchylomicronemia syndrome (1)  ·  Hyperlipoproteinemia Type I (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Dyslipidemias (1)  ·  Genetic Diseases, Inborn (1)  ·  Hyperlipidemias (1)  ·  Hyperlipoproteinemias (1)  ·  Lipid Metabolism Disorders (1)  ·  Lipid Metabolism, Inborn Errors (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nutritional and Metabolic Diseases (1)

Interventions

ISIS 304801 (1)

Sponsors

Akcea Therapeutics (1)

Countries

Brazil (1)  ·  Canada (1)  ·  France (1)  ·  Germany (1)  ·  Israel (1)  ·  Italy (1)  ·  Netherlands (1)  ·  South Africa (1)  ·  Spain (1)  ·  United Kingdom (1)  ·  United States (1)

NIH funding

2015 (1)