Leukodystrophy, Globoid Cell: Clinical Trials

1 trial for Leukodystrophy, Globoid Cell, newest first

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1 active not recruiting. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Active not recruiting 1
Phase 21Active not recruiting 1

Follow Leukodystrophy, Globoid Cell: new trials by email Literature Review of Leukodystrophy, Globoid Cell trials Research Report on Leukodystrophy, Globoid Cell

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Gene Transfer Clinical Trial for Infantile and Late Infantile Krabbe Disease Treated Previously With HSCT
FBX-101 - Krabbe Disease
Phase 1 / Phase 2Active not recruitingForge Biologics, Inc92023-02-032025-11-20

Narrower conditions

Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Demyelinating Diseases (1)  ·  Genetic Diseases, Inborn (1)  ·  Hereditary Central Nervous System Demyelinating Diseases (1)  ·  Leukoencephalopathies (1)  ·  Lipid Metabolism Disorders (1)  ·  Lipid Metabolism, Inborn Errors (1)  ·  Lipidoses (1)  ·  Lysosomal Storage Diseases (1)  ·  Lysosomal Storage Diseases, Nervous System (1)  ·  Metabolic Diseases (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Neurodegenerative Diseases (1)  ·  Nutritional and Metabolic Diseases (1)

Sponsors

Forge Biologics, Inc (1)

Countries

United States (1)

Results publications

PMID 36196048, PMID 39499628