1 withdrawn. 1 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Withdrawn 1 |
Follow Inborn Errors of Metabolism: new trials by email Literature Review of Inborn Errors of Metabolism trials Research Report on Inborn Errors of Metabolism
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Fetal Umbilical Cord Blood (UCB) Transplant for Lysosomal Storage Diseases ALD-601 - Lysosomal Storage Diseases, Inborn Errors of Metabolism | Phase 1 | Withdrawn | Joanne Kurtzberg, MD | 2009-10-01 | 2017-06-29 |
Gangliosidoses, GM2 (1) · Lysosomal Storage Diseases (1) · Metabolism, Inborn Errors (1) · Pelizaeus-Merzbacher Disease (1)
Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Demyelinating Diseases (1) · Gangliosidoses (1) · Genetic Diseases, Inborn (1) · Genetic Diseases, X-Linked (1) · Hereditary Central Nervous System Demyelinating Diseases (1) · Leukoencephalopathies (1) · Lipid Metabolism Disorders (1) · Lipid Metabolism, Inborn Errors (1) · Lipidoses (1) · Lysosomal Storage Diseases, Nervous System (1)
United States (1)