Hyperlipoproteinemia Type 1: Clinical Trials

1 trial for Hyperlipoproteinemia Type 1, newest first

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1 completed. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Completed 1

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Trials (filtered) newest first · largest first

All 1 trial

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TrialPhaseStatusSponsorEnrollmentStartUpdated
Phase 2 Study of AKCEA-ANGPTL3-LRx (ISIS 703802) in Participants With Familial Chylomicronemia Syndrome (FCS)
AKCEA-ANGPTL3-LRx - Familial Chylomicronemia Syndrome, Lipoprotein Lipase Deficiency
Phase 2CompletedAkcea Therapeutics32017-12-212021-01-07

Narrower conditions

Dyslipidemias (1)  ·  Familial hyperchylomicronemia syndrome (1)  ·  Genetic Diseases, Inborn (1)  ·  Hyperlipidemias (1)  ·  Hyperlipoproteinemia Type I (1)  ·  Hyperlipoproteinemias (1)  ·  Lipid Metabolism Disorders (1)  ·  Lipid Metabolism, Inborn Errors (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Nutritional and Metabolic Diseases (1)

Interventions

IONIS-ANGPTL3-LRx (1)  ·  vupanorsen (1)

Sponsors

Akcea Therapeutics (1)

Countries

Canada (1)