Hyperlipoproteinemia Type 1: Clinical Trials

2 trials for Hyperlipoproteinemia Type 1, newest first

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2 completed. 1 Phase 2, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 21Completed 1
Phase 31Completed 1

Follow Hyperlipoproteinemia Type 1: new trials by email Literature Review of Hyperlipoproteinemia Type 1 trials Research Report on Hyperlipoproteinemia Type 1

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Phase 2 Study of AKCEA-ANGPTL3-LRx (ISIS 703802) in Participants With Familial Chylomicronemia Syndrome (FCS)
AKCEA-ANGPTL3-LRx - Familial Chylomicronemia Syndrome, Lipoprotein Lipase Deficiency
Phase 2CompletedAkcea Therapeutics32017-12-212021-01-07
The Approach Open Label Study: A Study of Volanesorsen (Formerly IONIS-APOCIIIRx) in Participants With Familial Chylomicronemia Syndrome
Volanesorsen - Familial Chylomicronemia Syndrome, Lipoprotein Lipase Deficiency
Phase 3CompletedAkcea Therapeutics682015-12-232021-08-26

Narrower conditions

Familial hyperchylomicronemia syndrome (2)  ·  Hyperlipoproteinemia Type I (2)  ·  Dyslipidemias (1)  ·  Genetic Diseases, Inborn (1)  ·  Hyperlipidemias (1)  ·  Hyperlipoproteinemias (1)  ·  Lipid Metabolism Disorders (1)  ·  Lipid Metabolism, Inborn Errors (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Nutritional and Metabolic Diseases (2)  ·  Dyslipidemias (1)  ·  Genetic Diseases, Inborn (1)  ·  Hyperlipidemias (1)  ·  Hyperlipoproteinemias (1)  ·  Lipid Metabolism Disorders (1)  ·  Lipid Metabolism, Inborn Errors (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)

Interventions

IONIS-ANGPTL3-LRx (1)  ·  ISIS 304801 (1)  ·  vupanorsen (1)

Sponsors

Akcea Therapeutics (2)

Countries

Canada (2)  ·  Brazil (1)  ·  France (1)  ·  Germany (1)  ·  Israel (1)  ·  Italy (1)  ·  Netherlands (1)  ·  South Africa (1)  ·  Spain (1)  ·  United Kingdom (1)  ·  United States (1)

NIH funding

2015 (1)