1 recruiting. 1 Early Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Early Phase 1 | 1 | Recruiting 1 |
Follow Hyperchylomicronemia: new trials by email Literature Review of Hyperchylomicronemia trials Research Report on Hyperchylomicronemia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| CS-121 APOC3 Base Editing in Children and Adolescents With Hyperchylomicronemia CS-121 - Hyperchylomicronemia | Early Phase 1 | Recruiting | Shanghai Jiao Tong University School of Medicine | 15 | 2026-01-26 | 2026-01-28 |
Hyperlipoproteinemia Type I (1) · Pancreatitis (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Digestive System Diseases (1) · Dyslipidemias (1) · Genetic Diseases, Inborn (1) · Hyperlipidemias (1) · Hyperlipoproteinemias (1) · Lipid Metabolism Disorders (1) · Lipid Metabolism, Inborn Errors (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Nutritional and Metabolic Diseases (1) · Pancreatic Diseases (1)
Shanghai Jiao Tong University School of Medicine (1)
China (1)