Hereditary Angioedema: Clinical Trials

2 trials for Hereditary Angioedema, newest first

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2 enrolling by invitation. 2 Phase 3, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 32Enrolling by invitation 2
Phase 21Enrolling by invitation 1

Follow Hereditary Angioedema: new trials by email Literature Review of Hereditary Angioedema trials Research Report on Hereditary Angioedema

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Extension Study of Oral PHA-022121 for Acute Treatment of Angioedema Attacks in Patients With Hereditary Angioedema
deucrictibant - Hereditary Angioedema, Hereditary Angioedema Type I
Phase 2 / Phase 3Enrolling by invitationPharvaris Netherlands B.V.1502022-12-282026-07-21
Open-label Berotralstat Access to HAE Patients Previously Enrolled in Berotralstat Studies
berotralstat - Hereditary Angioedema, HAE
Phase 3Enrolling by invitationBioCryst Pharmaceuticals1392021-07-232025-12-23

Narrower conditions

Angioedemas, Hereditary (2)  ·  Hereditary Angioedema Type III (1)  ·  Hereditary Angioedema Types I and II (1)

Broader conditions

Angioedema (2)  ·  Cardiovascular Diseases (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Hereditary Complement Deficiency Diseases (2)  ·  Hypersensitivity (2)  ·  Hypersensitivity, Immediate (2)  ·  Immune System Diseases (2)  ·  Immunologic Deficiency Syndromes (2)  ·  Primary Immunodeficiency Diseases (2)  ·  Skin Diseases (2)  ·  Skin Diseases, Vascular (2)  ·  Skin and Connective Tissue Diseases (2)  ·  Urticaria (2)  ·  Vascular Diseases (2)

Interventions

berotralstat (1)

Sponsors

BioCryst Pharmaceuticals (1)  ·  Pharvaris Netherlands B.V. (1)

Countries

Canada (2)  ·  Czechia (2)  ·  France (2)  ·  Germany (2)  ·  Poland (2)  ·  South Africa (2)  ·  South Korea (2)  ·  Spain (2)  ·  United Kingdom (2)  ·  Argentina (1)  ·  Australia (1)  ·  Austria (1)  ·  Brazil (1)  ·  Bulgaria (1)  ·  Hong Kong (1)

Top investigators

Vesna Grivcheva-Panoska, MD, PhD (1)

NIH funding

2023 (1)