Genetics: Clinical Trials

1 trial for Genetics, newest first

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1 completed. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Completed 1

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Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study of Sirolimus Therapy for Segmental Overgrowth Caused by Somatic PI3K Activation
Sirolimus - PIK3CA-Related Overgrowth Spectrum (PROS), Growth Disorder
Phase 2CompletedNational Human Genome Research Institute (NHGRI)392015-04-232020-02-05

Narrower conditions

Congenital Abnormalities (1)  ·  Growth Disorders (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Pathologic Processes (1)  ·  Pathological Conditions, Signs and Symptoms (1)

Interventions

Sirolimus (1)

Sponsors

National Human Genome Research Institute (NHGRI) (1)

Countries

United States (1)

Top investigators

Kim M Keppler-Noreuil, M.D. (1)

Results publications

PMID 30270358