Genetic Diseases: Clinical Trials

1 trial for Genetic Diseases, newest first

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1 terminated. 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 11Terminated 1

Follow Genetic Diseases: new trials by email Literature Review of Genetic Diseases trials Research Report on Genetic Diseases

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Safety, Tolerability, Pharmacokinetics of ELX-02 in Healthy Adult Volunteers
ELX-02, Placebo - Genetic Diseases, Nonsense Mutations
Phase 1TerminatedEloxx Pharmaceuticals, Inc.422016-07-012019-10-22

Narrower conditions

Genetic Diseases, Inborn (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)

Interventions

ELX-02 (1)

Sponsors

Eloxx Pharmaceuticals, Inc. (1)