Familial Partial Lipodystrophy: Clinical Trials

1 trial for Familial Partial Lipodystrophy, newest first

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1 terminated. 1 Phase 2, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 21Terminated 1
Phase 31Terminated 1

Follow Familial Partial Lipodystrophy: new trials by email Literature Review of Familial Partial Lipodystrophy trials Research Report on Familial Partial Lipodystrophy

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
The BROADEN Study: A Study of Volanesorsen (Formerly IONIS-APOCIIIRx) in Participants With Familial Partial Lipodystrophy
volanesorsen, Placebo - Familial Partial Lipodystrophy
Phase 2 / Phase 3TerminatedAkcea Therapeutics402015-12-282021-10-18

Narrower conditions

Lipodystrophy, Familial Partial (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Laminopathies (1)  ·  Lipid Metabolism Disorders (1)  ·  Lipid Metabolism, Inborn Errors (1)  ·  Lipodystrophy (1)  ·  Metabolic Diseases (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Skin Diseases (1)  ·  Skin Diseases, Metabolic (1)  ·  Skin and Connective Tissue Diseases (1)

Interventions

ISIS 304801 (1)

Sponsors

Akcea Therapeutics (1)

Countries

Belgium (1)  ·  Brazil (1)  ·  Canada (1)  ·  Germany (1)  ·  Netherlands (1)  ·  Russia (1)  ·  United States (1)

Results publications

PMID 37164837

NIH funding

2015 (1)