1 recruiting. 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 1 | Recruiting 1 |
Follow Familial Partial Lipodystrophy: new trials by email Literature Review of Familial Partial Lipodystrophy trials Research Report on Familial Partial Lipodystrophy
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Open-label Extension Study to Evaluate Metreleptin in Patients With Partial Lipodystrophy Metreleptin - Familial Partial Lipodystrophy | Phase 3 | Recruiting | Chiesi Farmaceutici S.p.A. | 24 | 2024-10-14 | 2026-07-16 |
Lipodystrophy, Familial Partial (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Laminopathies (1) · Lipid Metabolism Disorders (1) · Lipid Metabolism, Inborn Errors (1) · Lipodystrophy (1) · Metabolic Diseases (1) · Nutritional and Metabolic Diseases (1) · Skin Diseases (1) · Skin Diseases, Metabolic (1) · Skin and Connective Tissue Diseases (1)
metreleptin (1)
Chiesi Farmaceutici S.p.A. (1)
United States (1)