Carnitine palmitoyl transferase 2 deficiency: Clinical Trials

2 trials for Carnitine palmitoyl transferase 2 deficiency, newest first

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2 completed. 2 Phase 2, 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 22Completed 2
Phase 11Completed 1

Follow Carnitine palmitoyl transferase 2 deficiency: new trials by email Literature Review of Carnitine palmitoyl transferase 2 deficiency trials Research Report on Carnitine palmitoyl transferase 2 deficiency

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Effect of Bezafibrate on Muscle Metabolism in Patients With Fatty Acid Oxidation Defects
Bezafibrate, Placebo - Carnitine Palmitoyltransferase II Deficiency, Very Long Chain Acyl Coa Dehydrogenase Deficiency
Phase 2CompletedCopenhagen University Hospital, Rigshospitalet122009-10-012012-05-30
High Protein Diet in Patients With Long-chain Fatty Acid Oxidation Disorders
Diet counseling - Very Long-chain Acyl-CoA Dehydrogenase Deficiency, Trifunctional Protein Deficiency
Phase 1 / Phase 2CompletedOregon Health and Science University132006-01-012020-04-29

Narrower conditions

VLCAD deficiency (2)  ·  Trifunctional Protein Deficiency With Myopathy And Neuropathy (1)

Interventions

Bezafibrate (1)  ·  Diet, Fat-Restricted (1)  ·  Diet, High-Protein (1)  ·  Diet, High-Protein Low-Carbohydrate (1)

Sponsors

Copenhagen University Hospital, Rigshospitalet (1)  ·  Oregon Health and Science University (1)

Countries

Denmark (1)