Activated PI3K-delta Syndrome: Clinical Trials

1 trial for Activated PI3K-delta Syndrome, newest first

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1 completed. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1
Phase 21Completed 1

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Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Rapamycin Treatment for Activated Phosphoinositide 3-Kinase δ Syndrome
Rapamycin - Activated PI3K-delta Syndrome, Immunodeficiency Primary
Phase 1 / Phase 2CompletedChildren's Hospital of Fudan University302017-12-012024-07-09

Narrower conditions

Primary Immunodeficiency Diseases (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Immune System Diseases (1)  ·  Immunologic Deficiency Syndromes (1)

Interventions

Sirolimus (1)

Sponsors

Children's Hospital of Fudan University (1)

Countries

China (1)

Top investigators

Jinqiao Sun, Ph.D.,M.D (1)