zodasiran: Clinical Trials

3 trials of zodasiran, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

2 active not recruiting, 1 recruiting. 3 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 33Active not recruiting 2, Recruiting 1

Follow zodasiran: new trials by email Literature Review of zodasiran trials Research Report on zodasiran

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study of Zodasiran in Adolescent Participants With Homozygous Familial Hypercholesterolemia
Zodasiran - Homozygous Familial Hypercholesterolemia
Phase 3RecruitingArrowhead Pharmaceuticals102026-10-012026-10-26
A Phase 3 Study of Zodasiran in Adolescent and Adult Subjects With Homozygous Familial Hypercholesterolemia (YOSEMITE)
zodasiran Injection, Placebo - Homozygous Familial Hypercholesterolemia
Phase 3Active not recruitingArrowhead Pharmaceuticals702025-06-172026-08-12
A Phase 3 Clinical Trial to Evaluate the Efficacy and Safety of VSA003 in Chinese HoFH Patients
VSA003, Placebo - Homozygous Familial Hypercholesterolemia (HoFH)
Phase 3Active not recruitingVisirna Therapeutics HK Limited462024-11-272026-05-05

Conditions studied

Homozygous Familial Hypercholesterolemia (3)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Dyslipidemias (1)  ·  Genetic Diseases, Inborn (1)  ·  Hyperlipidemias (1)  ·  Hyperlipoproteinemia Type II (1)  ·  Hyperlipoproteinemias (1)  ·  Lipid Metabolism Disorders (1)  ·  Lipid Metabolism, Inborn Errors (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nutritional and Metabolic Diseases (1)

Sponsors

Arrowhead Pharmaceuticals (2)  ·  Visirna Therapeutics HK Limited (1)

Countries

United States (2)  ·  Australia (1)  ·  Austria (1)  ·  Belgium (1)  ·  Brazil (1)  ·  Canada (1)  ·  China (1)  ·  Czechia (1)  ·  Denmark (1)  ·  France (1)  ·  Georgia (1)  ·  Germany (1)  ·  Israel (1)  ·  Japan (1)  ·  New Zealand (1)

NIH funding

2025 (1)