2 recruiting. 2 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 2 | Recruiting 2 |
Follow Sequencing Assay for Variant rs114518452: new trials by email Literature Review of Sequencing Assay for Variant rs114518452 trials Research Report on Sequencing Assay for Variant rs114518452
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Sickle Cell Disease autologous bone marrow derived CD34+ HSPCs electroporated with BCL11A enhancer targeting Cas9 ribonucleoprotein, Sequencing Assay for Variant rs114518452 - Sickle Cell Disease, Sickle Cell Anemia (HbSS, or HbSβ-thalassemia0) | Phase 1 | Recruiting | Daniel Bauer | 5 | 2026-08-01 | 2026-10-21 |
| Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies autologous bone marrow derived CD34+ HSPCs electroporated with BCL11A enhancer targeting Cas9 ribonucleoprotein, Sequencing Assay for Variant rs114518452 - Sickle Cell Disease, Sickle Cell Anemia (HbSS, or HbSβ-thalassemia0) | Phase 1 | Recruiting | Daniel Bauer | 10 | 2025-12-01 | 2026-02-03 |
Anemia, Sickle Cell (2) · beta-Thalassemia (1)
Daniel Bauer (2)
United States (2)