2 completed. 2 Phase 1, 2 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 2 | Completed 2 |
| Phase 2 | 2 | Completed 2 |
Follow pegademase bovine: new trials by email Literature Review of pegademase bovine trials Research Report on pegademase bovine
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Efficacy and Safety of the Cryopreserved Formulation of OTL-101 in Subjects With ADA-SCID Infusion of autologous cryopreserved EFS-ADA LV CD34+ cells (OTL-101), Busulfan, Peg-Ada - Severe Combined Immunodeficiency Due to ADA Deficiency | Phase 1 / Phase 2 | Completed | Great Ormond Street Hospital for Children NHS Foundation Trust | 13 | 2018-01-03 | 2023-02-01 |
| Lentiviral (LV) Gene Therapy for Adenosine Deaminase (ADA) Deficiency Infusion of autologous EFS-ADA LV CD34+ cells, Haematopoietic Stem Cell Transplantation (HSCT), Busulfan - Adenosine Deaminase Deficiency, Severe Combined Immunodeficiencies (SCID) | Phase 1 / Phase 2 | Completed | Great Ormond Street Hospital for Children NHS Foundation Trust | 36 | 2012-11-15 | 2021-09-16 |
Severe combined immunodeficiency due to adenosine deaminase deficiency (2) · Severe Combined Immunodeficiency (1)
Great Ormond Street Hospital for Children NHS Foundation Trust (2)
United Kingdom (2)
Claire Booth, Dr (2)