galsulfase: Clinical Trials

1 trial of galsulfase, newest first

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1 recruiting. 1 Phase 1.

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PhaseTrialsStatus
Phase 11Recruiting 1

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Trials (filtered) newest first · largest first

All 1 trial

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TrialPhaseStatusSponsorEnrollmentStartUpdated
PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
Aldurazyme (laronidase) - MPS I, MPS II
Phase 1RecruitingUniversity of California, San Francisco102021-07-012026-03-17

Conditions studied

Gaucher Disease (1)  ·  Mucopolysaccharidosis IV (1)  ·  Mucopolysaccharidosis VI (1)  ·  Mucopolysaccharidosis VII (1)  ·  Sudden Infant Death (1)  ·  Wolman Disease (1)

Sponsors

University of California, San Francisco (1)

Countries

United States (1)

Top investigators

Tippi MacKenzie, MD (1)

Results publications

PMID 15324318, PMID 19948615, PMID 21637107, PMID 23510062, PMID 28374935, PMID 28657663, PMID 30337566, PMID 32102934, PMID 37955580, PMID 39891377, PMID 9918480