3 terminated, 2 completed. 5 Phase 2, 2 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 5 | Terminated 3, Completed 2 |
| Phase 1 | 2 | Completed 1, Terminated 1 |
Follow GALNS protein, human: new trials by email Literature Review of GALNS protein, human trials Research Report on GALNS protein, human
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Efficacy and Safety Study of BMN 110 for Morquio A Syndrome Patients Who Have Limited Ambulation BMN 110 - Mucopolysaccharidosis IVA, Morquio A Syndrome | Phase 2 | Terminated | BioMarin Pharmaceutical | 16 | 2012-08-01 | 2016-01-12 |
| Safety and Exercise Study of Two Doses of BMN 110 for Morquio A Syndrome BMN 110 - Mucopolysaccharidosis IVA, Morquio A Syndrome | Phase 2 | Terminated | BioMarin Pharmaceutical | 25 | 2012-04-01 | 2016-02-01 |
| Study of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome) BMN 110 - Mucopolysaccharidosis IVA, Morquio A Syndrome | Phase 2 | Completed | BioMarin Pharmaceutical | 15 | 2011-10-01 | 2017-08-10 |
| A Study to Evaluate the Long-Term Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome) BMN 110 - MPS IV A, Mucopolysaccharidosis IVA | Phase 1 / Phase 2 | Terminated | BioMarin Pharmaceutical | 20 | 2010-11-01 | 2015-09-30 |
| A Study to Evaluate the Safety, Tolerability and Efficacy of BMN 110 in Subjects With Mucopolysaccharidosis IVA BMN 110 - MPS IV A | Phase 1 / Phase 2 | Completed | BioMarin Pharmaceutical | 20 | 2009-04-01 | 2014-06-30 |
Lysosomal Storage Diseases (5) · Mucopolysaccharidosis IV (5)
United Kingdom (5) · United States (3) · Germany (2) · Canada (1) · Italy (1) · Taiwan (1)
Celeste Decker, MD (2) · Adam Shaywitz, MD PhD (1) · Celeste Decker, M.D. (1) · Debra Lounsbury (1)