Ert: Clinical Trials

1 trial of Ert, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 completed. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Completed 1

Follow Ert: new trials by email Literature Review of Ert trials Research Report on Ert

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Long-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)
BMN 110 - Weekly, BMN 110 - Every Other Week - Mucopolysaccharidosis IV A, Morquio A Syndrome
Phase 3CompletedBioMarin Pharmaceutical1732011-07-012021-07-21

Conditions studied

Lysosomal Storage Diseases (1)  ·  Mucopolysaccharidosis IV (1)

Sponsors

BioMarin Pharmaceutical (1)

Countries

Argentina (1)  ·  Brazil (1)  ·  Canada (1)  ·  Colombia (1)  ·  Denmark (1)  ·  France (1)  ·  Germany (1)  ·  Italy (1)  ·  Japan (1)  ·  Netherlands (1)  ·  Norway (1)  ·  Portugal (1)  ·  Qatar (1)  ·  Saudi Arabia (1)  ·  South Korea (1)

Top investigators

Debra Lounsbury (1)

Results publications

PMID 27955919, PMID 28535791, PMID 29248359