donidalorsen: Clinical Trials

2 trials of donidalorsen, newest first

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2 completed. 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 22Completed 2

Follow donidalorsen: new trials by email Literature Review of donidalorsen trials Research Report on donidalorsen

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
An Extension Study of Donidalorsen (IONIS-PKK-LRx) in Participants With Hereditary Angioedema
Donidalorsen - Hereditary Angioedema
Phase 2CompletedIonis Pharmaceuticals, Inc.202020-03-312026-05-08
A Study to Assess the Clinical Efficacy of Donidalorsen (Also Known as IONIS-PKK-LRx and ISIS 721744) in Participants With Hereditary Angioedema
Donidalorsen, Placebo - Hereditary Angioedema
Phase 2CompletedIonis Pharmaceuticals, Inc.232020-01-072023-04-03

Conditions studied

Angioedemas, Hereditary (2)

Sponsors

Ionis Pharmaceuticals, Inc. (2)

Countries

Netherlands (2)  ·  United States (2)

Results publications

PMID 35294812, PMID 38009241, PMID 41802598

NIH funding

2019 (1)