AAVLK03hOTC: Clinical Trials

1 trial of AAVLK03hOTC, newest first

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1 recruiting. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Recruiting 1
Phase 21Recruiting 1

Follow AAVLK03hOTC: new trials by email Literature Review of AAVLK03hOTC trials Research Report on AAVLK03hOTC

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Halting Ornithine Transcarbamylase Deficiency With Recombinant AAV in ChildrEn
AAVLK03hOTC - Ornithine Transcarbamylase Deficiency
Phase 1 / Phase 2RecruitingUniversity College, London122023-11-012023-11-07

Conditions studied

Ornithine Carbamoyltransferase Deficiency Disease (1)

Sponsors

University College, London (1)

Countries

United Kingdom (1)

Top investigators

Federicco Mingozzi (1)