2 terminated. 2 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 2 | Terminated 2 |
Follow Propionic Acidemia: new trials by email Literature Review of Propionic Acidemia trials Research Report on Propionic Acidemia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Study of HST5040 in Subjects With Propionic or Methylmalonic Acidemia HST5040, Placebo - Methylmalonic Acidemia, Propionic Acidemia | Phase 2 | Terminated | HemoShear Therapeutics | 26 | 2021-03-15 | 2024-01-05 |
| Long-term Outcome of N-Carbamylglutamate Treatment in Propionic Acidemia and Methylmalonic Acidemia N-carbamylglutamate, Standard of Care - Propionic Acidemia, Methylmalonic Acidemia | Phase 2 | Terminated | Mendel Tuchman | 1 | 2012-09-01 | 2017-04-26 |
Methylmalonic acidemia (2) · Genetic Diseases, Inborn (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1)
Amino Acid Metabolism, Inborn Errors (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Nutritional and Metabolic Diseases (2) · Genetic Diseases, Inborn (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1)
N-carbamylglutamate (1) · Standard of Care (1) · carglumic acid (1)
HemoShear Therapeutics (1) · Mendel Tuchman (1)
United States (2) · Australia (1) · Saudi Arabia (1)
Mendel Tuchman, MD (1) · Patrick Horn, MD PhD (1)