Primary Immunodeficiency Diseases: Clinical Trials

1 trial for Primary Immunodeficiency Diseases, newest first

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1 suspended. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Suspended 1
Phase 21Suspended 1

Follow Primary Immunodeficiency Diseases: new trials by email Literature Review of Primary Immunodeficiency Diseases trials Research Report on Primary Immunodeficiency Diseases

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants
CL20-i4-EF1α-hγc-OPT, Busulfan, CliniMacs - Severe Combined Immunodeficiency Disease, X-linked
Phase 1 / Phase 2SuspendedSt. Jude Children's Research Hospital282016-08-172025-11-10

Narrower conditions

Immunologic Deficiency Syndromes (1)  ·  X-Linked Combined Immunodeficiency Diseases (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Immune System Diseases (1)  ·  Infant, Newborn, Diseases (1)  ·  Severe Combined Immunodeficiency (1)

Interventions

Busulfan (1)

Sponsors

St. Jude Children's Research Hospital (1)

Countries

United States (1)

Top investigators

Stephen Gottschalk, MD (1)

Results publications

PMID 30995372

NIH funding

P01HL053749 (1)