1 suspended. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Suspended 1 |
| Phase 2 | 1 | Suspended 1 |
Follow Primary Immunodeficiency Diseases: new trials by email Literature Review of Primary Immunodeficiency Diseases trials Research Report on Primary Immunodeficiency Diseases
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants CL20-i4-EF1α-hγc-OPT, Busulfan, CliniMacs - Severe Combined Immunodeficiency Disease, X-linked | Phase 1 / Phase 2 | Suspended | St. Jude Children's Research Hospital | 28 | 2016-08-17 | 2025-11-10 |
Immunologic Deficiency Syndromes (1) · X-Linked Combined Immunodeficiency Diseases (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Genetic Diseases, X-Linked (1) · Immune System Diseases (1) · Infant, Newborn, Diseases (1) · Severe Combined Immunodeficiency (1)
Busulfan (1)
St. Jude Children's Research Hospital (1)
United States (1)
P01HL053749 (1)