Primary Hyperoxaluria Type 3: Clinical Trials

1 trial for Primary Hyperoxaluria Type 3, newest first

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1 completed. 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1

Follow Primary Hyperoxaluria Type 3: new trials by email Literature Review of Primary Hyperoxaluria Type 3 trials Research Report on Primary Hyperoxaluria Type 3

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study to Evaluate Safety, Tolerability, PK and PD of DCR-PHXC in PH Type 3 Patients
DCR-PHXC, Sterile Normal Saline (0.9% NaCl) - Primary Hyperoxaluria Type 3
Phase 1CompletedDicerna Pharmaceuticals, Inc., a Novo Nordisk company62020-09-142024-09-19

Narrower conditions

Hyperoxaluria, Primary (1)

Broader conditions

Carbohydrate Metabolism, Inborn Errors (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Female Urogenital Diseases (1)  ·  Female Urogenital Diseases and Pregnancy Complications (1)  ·  Genetic Diseases, Inborn (1)  ·  Hyperoxaluria (1)  ·  Kidney Diseases (1)  ·  Male Urogenital Diseases (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Urogenital Diseases (1)  ·  Urologic Diseases (1)

Interventions

nedosiran (1)

Sponsors

Dicerna Pharmaceuticals, Inc., a Novo Nordisk company (1)

Countries

Germany (1)  ·  Netherlands (1)  ·  United Kingdom (1)  ·  United States (1)

Top investigators

Alexandra Haagensen, MD, MBA (1)