2 completed, 1 terminated. 2 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 2 | Completed 2 |
| Phase 2 | 1 | Terminated 1 |
Follow Nonsense Mutation: new trials by email Literature Review of Nonsense Mutation trials Research Report on Nonsense Mutation
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Phase 2 Study of ELX-02 in Patients With Nephropathic Cystinosis ELX-02 - Genetic Disease, Nonsense Mutation | Phase 2 | Terminated | Eloxx Pharmaceuticals, Inc. | 3 | 2019-08-02 | 2020-05-27 |
| Phase 1 Study of ELX-02 in Healthy Adult Subjects ELX-02, Placebo - Genetic Disease, Nonsense Mutation | Phase 1 | Completed | Eloxx Pharmaceuticals, Inc. | 62 | 2017-10-11 | 2021-03-16 |
| Phase 1 Study of ELX-02 in Healthy Adults Placebo, ELX-02 - Genetic Disease, Nonsense Mutation | Phase 1 | Completed | Eloxx Pharmaceuticals, Inc. | 18 | 2017-09-26 | 2023-08-22 |
Genetic Diseases, Inborn (3) · Cystinosis (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Lysosomal Storage Diseases (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Nutritional and Metabolic Diseases (1)
ELX-02 (3)
Eloxx Pharmaceuticals, Inc. (3)
Belgium (2) · Canada (1)
Paul Goodyer, MD (1)