Nijmegen Breakage Syndrome: Clinical Trials

3 trials for Nijmegen Breakage Syndrome, newest first

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1 not yet recruiting, 1 recruiting, 1 unknown. 3 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 23Not yet recruiting 1, Recruiting 1, Unknown 1

Follow Nijmegen Breakage Syndrome: new trials by email Literature Review of Nijmegen Breakage Syndrome trials Research Report on Nijmegen Breakage Syndrome

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study of Treosulfan-Based Conditioning for HSCT in Nijmegen Breakage Syndrome
Treosulfan (Treo) - HSCT, Nijmegen Breakage Syndrome
Phase 2Not yet recruitingFederal Research Institute of Pediatric Hematology, Oncology and Immunology242025-12-302026-01-05
Low Dose Treosulfan Based Conditioning Regimen and PTCy in HSCT for Nijmegen Breakage Syndrome
Treosulfan - Nijmegen Breakage Syndrome
Phase 2RecruitingFederal Research Institute of Pediatric Hematology, Oncology and Immunology102023-11-222024-01-10
Low Dose Treosulfan Based Conditioning Regimen in HSCT for Nijmegen Breakage Syndrome
Treosulfan - Nijmegen Breakage Syndrome
Phase 2UnknownFederal Research Institute of Pediatric Hematology, Oncology and Immunology102020-05-222020-06-25

Broader conditions

DNA Repair-Deficiency Disorders (3)  ·  Metabolic Diseases (3)  ·  Nutritional and Metabolic Diseases (3)

Interventions

treosulfan (3)

Sponsors

Federal Research Institute of Pediatric Hematology, Oncology and Immunology (3)

Countries

Russia (2)