1 enrolling by invitation. 1 Phase 4.
| Phase | Trials | Status |
|---|---|---|
| Phase 4 | 1 | Enrolling by invitation 1 |
Follow Mucinoses: new trials by email Literature Review of Mucinoses trials Research Report on Mucinoses
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Safety, Tolerability and Efficacy of ICV AX 250 Treatment in MPS IIIB -OLE AX 250 - MPS III B | Phase 4 | Enrolling by invitation | Allievex Corporation | 15 | 2022-12-02 | 2023-08-09 |
Carbohydrate Metabolism, Inborn Errors (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Connective Tissue Diseases (1) · Genetic Diseases, Inborn (1) · Lysosomal Storage Diseases (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Mucopolysaccharidoses (1) · Nutritional and Metabolic Diseases (1) · Skin and Connective Tissue Diseases (1)
Colombia (1) · Germany (1) · Turkey (Türkiye) (1) · United Kingdom (1) · United States (1)