Mucinoses: Clinical Trials

1 trial for Mucinoses, newest first

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1 enrolling by invitation. 1 Phase 4.

By phase and status

PhaseTrialsStatus
Phase 41Enrolling by invitation 1

Follow Mucinoses: new trials by email Literature Review of Mucinoses trials Research Report on Mucinoses

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Safety, Tolerability and Efficacy of ICV AX 250 Treatment in MPS IIIB -OLE
AX 250 - MPS III B
Phase 4Enrolling by invitationAllievex Corporation152022-12-022023-08-09

Narrower conditions

Mucopolysaccharidosis III (1)

Broader conditions

Carbohydrate Metabolism, Inborn Errors (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Connective Tissue Diseases (1)  ·  Genetic Diseases, Inborn (1)  ·  Lysosomal Storage Diseases (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Mucopolysaccharidoses (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Skin and Connective Tissue Diseases (1)

Sponsors

Allievex Corporation (1)

Countries

Colombia (1)  ·  Germany (1)  ·  Turkey (Türkiye) (1)  ·  United Kingdom (1)  ·  United States (1)