1 terminated. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Terminated 1 |
| Phase 2 | 1 | Terminated 1 |
Follow MPS IIIA: new trials by email Literature Review of MPS IIIA trials Research Report on MPS IIIA
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Gene Transfer Study of ABO-102 in Patients With Middle and Advanced Phases of MPS IIIA Disease ABO-102 - MPS IIIA, Sanfilippo Syndrome | Phase 1 / Phase 2 | Terminated | Ultragenyx Pharmaceutical Inc | 5 | 2019-09-18 | 2023-07-25 |
Carbohydrate Metabolism, Inborn Errors (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Connective Tissue Diseases (1) · Genetic Diseases, Inborn (1) · Lysosomal Storage Diseases (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Mucinoses (1) · Mucopolysaccharidoses (1) · Nutritional and Metabolic Diseases (1) · Skin and Connective Tissue Diseases (1)
Ultragenyx Pharmaceutical Inc (1)
Australia (1) · Spain (1) · United States (1)
2018 (1)