Methylmalonic Acidemia (MMA): Clinical Trials

2 trials for Methylmalonic Acidemia (MMA), newest first

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2 withdrawn. 2 Phase 1, 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 12Withdrawn 2
Phase 22Withdrawn 2

Follow Methylmalonic Acidemia (MMA): new trials by email Literature Review of Methylmalonic Acidemia (MMA) trials Research Report on Methylmalonic Acidemia (MMA)

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study to Evaluate the Safety, Tolerability, and Pharmacodynamics of SEL-302 in Pediatric Subjects With MMA
SEL-302 - Methylmalonic Acidemia (MMA)
Phase 1 / Phase 2WithdrawnSelecta Biosciences, Inc.2022-12-192024-09-24
Open Label Study of mRNA-3704 in Patients With Isolated Methylmalonic Acidemia
mRNA-3704 - Methylmalonic Acidemia (MMA), Metabolism, Inborn Errors
Phase 1 / Phase 2WithdrawnModernaTX, Inc.2019-05-282020-11-13

Narrower conditions

Methylmalonic acidemia (2)  ·  Metabolism, Inborn Errors (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Metabolic Diseases (1)  ·  Nutritional and Metabolic Diseases (1)

Sponsors

ModernaTX, Inc. (1)  ·  Selecta Biosciences, Inc. (1)

Countries

United States (1)