Medium chain acyl CoA dehydrogenase deficiency: Clinical Trials

1 trial for Medium chain acyl CoA dehydrogenase deficiency, newest first

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1 completed. 1 Phase 1.

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PhaseTrialsStatus
Phase 11Completed 1

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Trials (filtered) newest first · largest first

All 1 trial

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TrialPhaseStatusSponsorEnrollmentStartUpdated
Use of Ravictiâ„¢ in Patients With MCAD Deficiency With the 985A>G (K304E) Mutation
Ravicti - Medium-chain Acyl-CoA Dehydrogenase (MCAD) Deficiency
Phase 1CompletedUniversity of Pittsburgh42013-06-012017-09-25

Interventions

glycerol phenylbutyrate (1)

Sponsors

University of Pittsburgh (1)

Countries

United States (1)

Top investigators

Gerard Vockley, MD, PhD (1)