1 unknown. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Unknown 1 |
| Phase 2 | 1 | Unknown 1 |
Follow LGMD: new trials by email Literature Review of LGMD trials Research Report on LGMD
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Evaluating Safety and Efficacy of Autologous Gene-edited Muscle Stem Cells (GenPHSats-bASKet) GenPHSat injection (Safety), GenPHSat injection (Efficacy), Muscle Biopsy (Safety) - LGMD | Phase 1 / Phase 2 | Unknown | Simone Spuler, MD | 6 | 2024-07-01 | 2023-08-03 |
Safety (1)