LGMD: Clinical Trials

1 trial for LGMD, newest first

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1 unknown. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Unknown 1
Phase 21Unknown 1

Follow LGMD: new trials by email Literature Review of LGMD trials Research Report on LGMD

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Evaluating Safety and Efficacy of Autologous Gene-edited Muscle Stem Cells (GenPHSats-bASKet)
GenPHSat injection (Safety), GenPHSat injection (Efficacy), Muscle Biopsy (Safety) - LGMD
Phase 1 / Phase 2UnknownSimone Spuler, MD62024-07-012023-08-03

Interventions

Safety (1)

Sponsors

Simone Spuler, MD (1)

Top investigators

Simone Spuler, Prof Dr med (1)