Hypotonia Cystinuria Syndrome: Clinical Trials

1 trial for Hypotonia Cystinuria Syndrome, newest first

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1 unknown. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Unknown 1

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Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Sulfamethoxazole for the Treatment of Primary PREPL Deficiency
Sulfamethoxazole - Hypotonia Cystinuria Syndrome, Isolated PREPL Deficiency
Phase 2UnknownUniversitair Ziekenhuis Brussel152015-10-012015-12-29

Narrower conditions

Hypotonia-Cystinuria Syndrome (1)

Interventions

Sulfamethoxazole (1)

Sponsors

Universitair Ziekenhuis Brussel (1)