1 completed, 1 recruiting. .
Follow Ceroid lipofuscinosis, neuronal 5: new trials by email Literature Review of Ceroid lipofuscinosis, neuronal 5 trials Research Report on Ceroid lipofuscinosis, neuronal 5
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Natural History and Longitudinal Clinical Assessments in NCL / Batten Disease, the International DEM-CHILD Database Natural History - Neuronal Ceroid Lipofuscinosis, Batten Disease | Recruiting | Universitätsklinikum Hamburg-Eppendorf | 500 | 2020-04-08 | 2021-10-29 | |
| A Natural History Study of Neuronal Ceroid Lipofuscinosis Type 5 (CLN5) Ceroid Lipofuscinosis, Neuronal 5 | Completed | Neurogene Inc. | 37 | 2019-03-13 | 2024-06-27 |
Kufor-Rakeb syndrome (1) · Lysosomal Storage Diseases (1) · Metabolic Diseases (1) · Neurodegenerative Diseases (1) · Neuronal Ceroid-Lipofuscinoses (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Heredodegenerative Disorders, Nervous System (1) · Lipid Metabolism Disorders (1) · Lipid Metabolism, Inborn Errors (1) · Lipidoses (1) · Metabolism, Inborn Errors (1) · Nervous System Diseases (1) · Nutritional and Metabolic Diseases (1)
Neurogene Inc. (1) · Universitätsklinikum Hamburg-Eppendorf (1)
Germany (1) · United States (1)
Angela Schulz, MD, PhD (1) · Elise Beausoleil (1)