Biotinidase Deficiency: Clinical Trials

1 trial for Biotinidase Deficiency, newest first

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1 completed. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1
Phase 21Completed 1

Follow Biotinidase Deficiency: new trials by email Literature Review of Biotinidase Deficiency trials Research Report on Biotinidase Deficiency

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study of ORL-1B in Patients With Biotinidase Deficiency
ORL-1B - Biotinidase Deficiency
Phase 1 / Phase 2CompletedOrpha Labs202013-08-312018-01-17

Broader conditions

Amino Acid Metabolism, Inborn Errors (1)  ·  Carbohydrate Metabolism, Inborn Errors (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Multiple Carboxylase Deficiency (1)  ·  Nutritional and Metabolic Diseases (1)

Sponsors

Orpha Labs (1)