1 terminated. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Terminated 1 |
| Phase 2 | 1 | Terminated 1 |
Follow Aase Smith syndrome 2: new trials by email Literature Review of Aase Smith syndrome 2 trials Research Report on Aase Smith syndrome 2
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Safety and Efficacy Study of Sotatercept in Adults With Transfusion Dependent Diamond Blackfan Anemia Sotatercept, Sotatercept with prednisone boost - Diamond Blackfan Anemia | Phase 1 / Phase 2 | Terminated | Northwell Health | 19 | 2012-01-01 | 2023-03-17 |
Anemia, Diamond-Blackfan (1) · Anemia, Hypoplastic, Congenital (1) · Bone Marrow Failure Disorders (1) · Red-Cell Aplasia, Pure (1)
Anemia (1) · Anemia, Aplastic (1) · Bone Marrow Diseases (1) · Congenital Bone Marrow Failure Syndromes (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Hematologic Diseases (1) · Hemic and Lymphatic Diseases (1)
ACE-011 (1) · Prednisone (1)
Northwell Health (1)
United States (1)