Splice Bio: Clinical Trials

2 trials sponsored by Splice Bio, newest first

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2 recruiting. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Recruiting 1
Phase 21Recruiting 1

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Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Phase 1/2, First-in-Human Dose Escalation/Expansion Study to Evaluate the Safety, Tolerability and Preliminary Efficacy of a Subretinal Injection of SB-007 in Subjects With Stargardt Disease (STGD1)
SB-007 - Stargardt Disease, Stargardt Macular Degeneration
Phase 1 / Phase 2RecruitingSplice Bio572025-02-112025-04-29
An Observational Study in Subjects to Follow the Progression of Stargardt Disease Type 1 (STGD1) Caused by Bi-Allelic Autosomal Recessive Mutations in the ABCA4 Gene
Stargardt, Stargardt's Disease
RecruitingSplice Bio752024-03-292025-09-19

Conditions studied

Stargardt Disease (2)

Countries

United States (2)  ·  Germany (1)  ·  United Kingdom (1)