Roy E. Weiss, M.D.: Clinical Trials

1 trial sponsored by Roy E. Weiss, M.D., newest first

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1 available. .

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TrialPhaseStatusSponsorEnrollmentStartUpdated
Rescue of Infants With MCT8 Deficiency
Diiodothyropropionic acid (DITPA) - Mct8 (Slc16A2)-Specific Thyroid Hormone Cell Transporter Deficiency
AvailableRoy E. Weiss, M.D.2025-12-11

Conditions studied

Allan-Herndon-Dudley syndrome (1)

Interventions

3,5-diiodothyropropionic acid (1)

Countries

United States (1)

Top investigators

Roy E Weiss, M.D. (1)