Pharming Technologies B.V.: Clinical Trials

1 trial sponsored by Pharming Technologies B.V., newest first

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1 unknown. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Unknown 1

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Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
An Open-Label Study to Assess the Safety & Efficacy of Leniolisib in Japanese Patients With APDS
Leniolisib - APDS Gene Mutation
Phase 3UnknownPharming Technologies B.V.32023-08-032024-02-08

Interventions

leniolisib (1)

Countries

Japan (1)

Top investigators

Hirokazu Kanegane, Prof. (1)