3 completed, 1 terminated. 2 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 2 | Completed 1, Terminated 1 |
| Phase 2 | 1 | Completed 1 |
Follow Audentes Therapeutics: new trials by email
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| AAV9 U7snRNA Gene Therapy to Treat Boys With DMD Exon 2 Duplications. scAAV9.U7.ACCA - Duchenne Muscular Dystrophy | Phase 1 / Phase 2 | Completed | Megan Waldrop | 3 | 2020-01-15 | 2025-09-11 |
| Gene Transfer Clinical Study in Crigler-Najjar Syndrome AT342 - Crigler-Najjar Syndrome | Phase 1 | Terminated | Audentes Therapeutics | 1 | 2017-09-08 | 2022-05-18 |
| Clinical Assessment Study in Crigler-Najjar Syndrome Crigler-Najjar Syndrome | Completed | Audentes Therapeutics | 8 | 2017-03-10 | 2019-02-06 | |
| Respiratory Muscle Function in Untreated X-Linked Myotubular Myopathy (XLMTM) History and physical, Tidal breathing, Maximal respiratory pressures - X-linked Myotubular Myopathy | Completed | University of Florida | 28 | 2015-10-01 | 2021-02-15 |
Crigler-Najjar Syndrome (2) · Muscular Dystrophy, Duchenne (1) · Myopathies, Structural, Congenital (1)
Health Records, Personal (1) · Restraint, Physical (1)
United States (4) · Israel (2) · United Kingdom (2)
Barbara K Smith, PT, PhD (1) · Megan Waldrop, MD (1) · Suyash Prasad, M.D. (1) · Suyash Prasad, MBBS, MRCP,MRCPCH, FFPM (1)