Venglustat GZ402671: Clinical Trials

2 trials of Venglustat GZ402671, newest first

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2 terminated. 2 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 32Terminated 2

Follow Venglustat GZ402671: new trials by email Literature Review of Venglustat GZ402671 trials Research Report on Venglustat GZ402671

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Long-term Treatment of Autosomal Dominant Polycystic Kidney Disease (ADPKD) With Venglustat
Venglustat GZ402671 - Congenital Cystic Kidney Disease
Phase 3TerminatedSanofi242021-02-092025-09-17
A Multinational, Randomized, Double-blind, Placebo-controlled Study to Assess the Efficacy, Pharmacodynamics, Pharmacokinetics, and Safety of Venglustat in Late-onset GM2
venglustat GZ402671, placebo - Tay-Sachs Disease, Sandhoff Disease
Phase 3TerminatedGenzyme, a Sanofi Company752020-06-292026-01-28

Conditions studied

Kidney Diseases, Cystic (1)  ·  Sandhoff Disease (1)  ·  Tay-Sachs Disease (1)

Sponsors

Genzyme, a Sanofi Company (1)  ·  Sanofi (1)

Countries

Germany (2)  ·  Japan (2)  ·  Spain (2)  ·  United States (2)  ·  Argentina (1)  ·  Australia (1)  ·  Belgium (1)  ·  Brazil (1)  ·  Czechia (1)  ·  France (1)  ·  Italy (1)  ·  Netherlands (1)  ·  Portugal (1)  ·  Russia (1)  ·  South Korea (1)

Results publications

PMID 34539759

NIH funding

2019 (1)