3 completed, 2 recruiting. 2 Phase 2, 2 Phase 3, 1 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 2 | Completed 2 |
| Phase 3 | 2 | Completed 1, Recruiting 1 |
| Phase 1 | 1 | Completed 1 |
Follow sepiapterin: new trials by email Literature Review of sepiapterin trials Research Report on sepiapterin
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Impact Of A Phe-Restricted Diet On Gut Health In Children With PKU Phenylalanine-restricted diet alone, Sapropterin Dihydrochloride, Sepiapterin - Phenylketonuria | Recruiting | Birmingham Women's and Children's NHS Foundation Trust | 148 | 2025-10-01 | 2026-10-06 | |
| A Study of Sepiapterin in Participants With Phenylketonuria (PKU) Sepiapterin - Phenylketonuria | Phase 3 | Recruiting | PTC Therapeutics | 56 | 2024-03-04 | 2026-10-23 |
| A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria PTC923 - Phenylketonuria | Phase 3 | Completed | PTC Therapeutics | 247 | 2022-02-14 | 2026-09-09 |
| A Study of CNSA-001 in Women With Diabetic Gastroparesis CNSA-001, Placebo - Gastroparesis | Phase 2 | Completed | PTC Therapeutics | 21 | 2019-02-27 | 2022-01-05 |
| A Study of PTC923 (CNSA-001) in Primary Tetrahydrobiopterin (BH4) Deficient Participants With Hyperphenylalaninemia PTC923 - BH4 Deficiency, Hyperphenylalaninemia | Phase 1 / Phase 2 | Completed | PTC Therapeutics | 8 | 2019-01-03 | 2023-11-14 |
Phenylketonurias (4) · Gastroparesis (1)
PTC Therapeutics (4) · Birmingham Women's and Children's NHS Foundation Trust (1)
United States (4) · United Kingdom (3) · Australia (2) · France (2) · Poland (2) · Brazil (1) · Canada (1) · Czechia (1) · Denmark (1) · Georgia (1) · Germany (1) · Ireland (1) · Italy (1) · Japan (1) · Mexico (1)
Neil Smith, PharmD (2) · Anita MacDonald, PhD (1)
2023 (1)