rAAV9.CMV.hNAGLU: Clinical Trials

1 trial of rAAV9.CMV.hNAGLU, newest first

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1 terminated. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Terminated 1
Phase 21Terminated 1

Follow rAAV9.CMV.hNAGLU: new trials by email Literature Review of rAAV9.CMV.hNAGLU trials Research Report on rAAV9.CMV.hNAGLU

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Gene Transfer Clinical Trial for Mucopolysaccharidosis (MPS) IIIB
rAAV9.CMV.hNAGLU - Mucopolysaccharidosis Type 3 B
Phase 1 / Phase 2TerminatedAbeona Therapeutics, Inc112017-10-162022-05-05

Conditions studied

Mucopolysaccharidosis III (1)

Sponsors

Abeona Therapeutics, Inc (1)

Countries

France (1)  ·  Germany (1)  ·  Spain (1)  ·  United States (1)

Results publications

PMID 32884151