rAAV-Olig001-ASPA: Clinical Trials

1 trial of rAAV-Olig001-ASPA, newest first

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1 enrolling by invitation. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Enrolling by invitation 1
Phase 21Enrolling by invitation 1

Follow rAAV-Olig001-ASPA: new trials by email Literature Review of rAAV-Olig001-ASPA trials Research Report on rAAV-Olig001-ASPA

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
rAAV-Olig001-ASPA Gene Therapy for Treatment of Children With Typical Canavan Disease
rAAV-Olig001-ASPA, Levetiracetam, Prednisone - Canavan Disease
Phase 1 / Phase 2Enrolling by invitationMyrtelle Inc.242021-04-012025-11-14

Conditions studied

Canavan Disease (1)

Sponsors

Myrtelle Inc. (1)

Countries

United States (1)

Top investigators

Robert Lober, MD, PhD (1)

Results publications

PMID 40957959