HST5040: Clinical Trials

1 trial of HST5040, newest first

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1 terminated. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Terminated 1

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Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study of HST5040 in Subjects With Propionic or Methylmalonic Acidemia
HST5040, Placebo - Methylmalonic Acidemia, Propionic Acidemia
Phase 2TerminatedHemoShear Therapeutics262021-03-152024-01-05

Conditions studied

Genetic Diseases, Inborn (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Methylmalonic acidemia (1)  ·  Propionic Acidemia (1)

Sponsors

HemoShear Therapeutics (1)

Countries

Australia (1)  ·  Saudi Arabia (1)  ·  United States (1)

Top investigators

Patrick Horn, MD PhD (1)