Genes: Clinical Trials

1 trial of Genes, newest first

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1 enrolling by invitation. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Enrolling by invitation 1
Phase 21Enrolling by invitation 1

Follow Genes: new trials by email Literature Review of Genes trials Research Report on Genes

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Part B- G1X-CGD (Lentiviral Vector Transduced CD34+ Cells) in Patients With X-Linked Chronic Granulomatous Disease
Busulfan, Tocilizumab, Eltrombopag - Chronic Granulomatous Disease (CGD)
Phase 1 / Phase 2Enrolling by invitationNational Institute of Allergy and Infectious Diseases (NIAID)102025-09-102026-09-08

Conditions studied

Granulomatous Disease, Chronic (1)

Sponsors

National Institute of Allergy and Infectious Diseases (NIAID) (1)

Countries

United States (1)

Top investigators

Elizabeth M Kang, M.D. (1)